Antenatal cell gene transfer: an immunological Trojan horse?

This publication has 14 references indexed in Scilit:

• Sustained high-level expression of human factor IX (hFIX) after liver-targeted delivery of recombinant adeno-associated virus encoding the hFIX gene in rhesus macaques
  Blood, 2002
• Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy
  Blood, 2002
• Muscle-Directed Gene Transfer and Transient Immune Suppression Result in Sustained Partial Correction of Canine Hemophilia B Caused by a Null Mutation
  Molecular Therapy, 2001
• Nonviral Transfer of the Gene Encoding Coagulation Factor VIII in Patients with Severe Hemophilia A
  New England Journal of Medicine, 2001
• The Malmö International Brother Study (MIBS): further support for genetic predisposition to inhibitor development
  Haemophilia, 2001
• Systemic delivery of an adenoviral vector encoding canine factor VIII results in short-term phenotypic correction, inhibitor development, and biphasic liver toxicity in hemophilia A dogs
  Blood, 2001
• Oral immune tolerance induction to factor VIII via breast milk, a possibility?
  Haemophilia, 2000
• Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
  Nature Genetics, 2000
• Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector
  Nature Medicine, 1999
• Histocompatibility antigen patterns in haemophilic patients with factor VIII antibodies
  British Journal of Haematology, 1990