Adeno-associated Virus 2-Mediated Transduction and Erythroid Lineage-Restricted Long-Term Expression of the Human β-Globin Gene in Hematopoietic Cells from Homozygous β-Thalassemic Mice
Open Access
- 1 June 2001
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 3 (6) , 940-946
- https://doi.org/10.1006/mthe.2001.0346
Abstract
No abstract availableKeywords
This publication has 41 references indexed in Scilit:
- Adeno-associated virus 2-mediated gene transfer in vivo: organ-tropism and expression of transduced sequences in miceGene, 1997
- Biology of Adeno-associated VirusPublished by Springer Nature ,1996
- Generation of a high-titer retroviral vector capable of expressing high levels of the human beta-globin gene.Proceedings of the National Academy of Sciences, 1995
- Suppression of human alpha-globin gene expression mediated by the recombinant adeno-associated virus 2-based antisense vectors.The Journal of Experimental Medicine, 1994
- Gene Therapy for Human HemoglobinopathiesExperimental Biology and Medicine, 1993
- Use of Adeno-Associated Virus as a General Transduction Vector for Mammalian CellsPublished by Springer Nature ,1992
- Mapping and direct visualization of a region-specific viral DNA integration site on chromosome 19q13-qterGenomics, 1991
- Globin gene regulation and switching: Circa 1990Cell, 1990
- Parvovirus replicationMicrobiological Reviews, 1990
- An erythroid-specific, developmental-stage-independent enhancer far upstream of the human "beta-like globin" genes.Proceedings of the National Academy of Sciences, 1989