Good News for Gene Therapy
- 15 April 2004
- journal article
- Published by Massachusetts Medical Society in New England Journal of Medicine
- Vol. 350 (16) , 1679-1680
- https://doi.org/10.1056/nejmcibr040341
Abstract
The promise of gene therapy has been dimmed in the past few years by a number of setbacks, including the development of T-cell leukemia in infants treated for severe combined immunodeficiency. A recent study suggests that these cases do not augur ill for the field as a whole and that specific changes to gene-therapy protocols may reduce the chances that such therapy will inadvertently trigger cancer.Keywords
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