THE EFFECT OF ACTH IN A CASE OF CEREBROMACULAR DEGENERATION (TAY-SACHS DISEASE): AN ENDOCRINOLOGIC STUDY

Abstract
An 18-month-old female child with cerebromacular degeneration (Tay-Sachs disease) received 1000 mg. of ACTH over a period of 24 days in doses of 25 to 50 mg. daily. The adrenal cortex reacted normally, as demonstrated by hyperglycemia, eosinopenia, leukocytosis, and elevated urinary excretion of estrogens, 17-ketosteroids, and formaldehydogenic corticoids. The initially elevated lipid P was reduced approximately 60%. Serum cholesterol initially at a normal level, was also decreased under therapy. The blood and urine citrates were markedly depressed. Clinically, no significant changes were observed. The usual course of the disease was not altered.

This publication has 1 reference indexed in Scilit: