Dystonia in the Mohr–Tranebjaerg syndrome responds to GABAergic substances

Abstract
Mutations in the X‐linked deafness–dystonia peptide 1 (DDP1) gene cause Mohr–Tranebjaerg syndrome (MTS), a rare form of deafness associated with dystonia. In the patient presented here, improvement of dystonic symptoms upon treatment with alcohol and GABAergic substances is demonstrated for the first time. © 2004 Movement Disorder Society