Efficient production of human FVIII in hemophilic mice using lentiviral vectors
Open Access
- 1 May 2003
- journal article
- research article
- Published by Elsevier in Molecular Therapy
- Vol. 7 (5) , 623-631
- https://doi.org/10.1016/s1525-0016(03)00073-x
Abstract
No abstract availableKeywords
This publication has 43 references indexed in Scilit:
- Tissue Distribution of Factor VIII Gene Expression In Vivo – A Closer LookThrombosis and Haemostasis, 2001
- Long-Term Persistence of Human Bone Marrow Stromal Cells Transduced with Factor VIII-Retroviral Vectors and Transient Production of Therapeutic Levels of Human Factor VIII in Nonmyeloablated Immunodeficient MiceHuman Gene Therapy, 2000
- Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia AProceedings of the National Academy of Sciences, 1998
- Gene therapy for hemophilia A: production of therapeutic levels of human factor VIII in vivo in mice.Proceedings of the National Academy of Sciences, 1995
- In vivo production of human factor VII in mice after intrasplenic implantation of primary fibroblasts transfected by receptor-mediated, adenovirus-augmented gene delivery.Proceedings of the National Academy of Sciences, 1994
- Toward Gene Therapy for Hemophilia A: Long-Term Persistence of Factor VIII-Secreting Fibroblasts after Transplantation into Immunodeficient MiceHuman Gene Therapy, 1993
- The molecular basis of hemophilia A in manTrends in Genetics, 1988
- Ultrastructural localization of factor VIII procoagulant antigen in human liver hepatocytesNature, 1985
- Distribution of factor VIII mRNA and antigen in human liver and other tissuesNature, 1985
- Detection of factor VIII/coagulant antigen in human liver tissueNature, 1983