Design of Tissue-specific Regulatory Cassettes for High-level rAAV-mediated Expression in Skeletal and Cardiac Muscle
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Open Access
- 1 February 2007
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 15 (2) , 320-329
- https://doi.org/10.1038/sj.mt.6300027
Abstract
No abstract availableKeywords
This publication has 46 references indexed in Scilit:
- Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8Molecular Therapy, 2006
- Sustained Whole-Body Functional Rescue in Congestive Heart Failure and Muscular Dystrophy Hamsters by Systemic Gene TransferCirculation, 2005
- Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoterMolecular Therapy, 2005
- Sustained correction of glycogen storage disease type II using adeno-associated virus serotype 1 vectorsGene Therapy, 2005
- Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heartNature Biotechnology, 2005
- Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6Molecular Therapy, 2004
- Systemic delivery of genes to striated muscles using adeno-associated viral vectorsNature Medicine, 2004
- Several Log Increase in Therapeutic Transgene Delivery by Distinct Adeno-Associated Viral Serotype VectorsMolecular Therapy, 2000
- Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vectorNature Medicine, 1999
- Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic proteinProceedings of the National Academy of Sciences, 1996