Discussion

• 15 August 1998
• journal article
• editorial
• Published by Elsevier in Biochemical Pharmacology
• Vol. 56  (4) , 421-430
• https://doi.org/10.1016/s0006-2952(98)00115-4

Abstract

Keywords

• GENE THERAPY
• BONE MARROW
• TREATMENT
• LYSOSOMES
• REPLACEMENT
• GLYCOSPHINGOLIPID
• FUNCTIONAL
• MODEL
• STORAGE
• FULLY