Bicistronic lentiviral vector corrects β-hexosaminidase deficiency in transduced and cross-corrected human Sandhoff fibroblasts
- 13 June 2005
- journal article
- Published by Elsevier in Neurobiology of Disease
- Vol. 20 (2) , 583-593
- https://doi.org/10.1016/j.nbd.2005.04.017
Abstract
No abstract availableKeywords
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