Impact of 144 weeks of laronidase therapy on body functions, endurance and general well‐being in a Hurler–Scheie patient
- 8 July 2006
- journal article
- case report
- Published by Wiley in Journal of Inherited Metabolic Disease
- Vol. 29 (4) , 590
- https://doi.org/10.1007/s10545-006-0329-5
Abstract
The quality of life of a Hurler–Scheie patient who experienced improvement in several organ functions and regained mobility after 144 weeks of laronidase enzyme replacement therapy is described.Keywords
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