Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver
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Open Access
- 1 April 2006
- journal article
- Published by American Society of Hematology in Blood
- Vol. 107 (7) , 2653-2661
- https://doi.org/10.1182/blood-2005-10-4035
Abstract
Transduction with recombinant adeno-associated virus (AAV) vectors is limited by the need to convert its single-stranded (ss) genome to transcriptionKeywords
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