Targeting Gene Therapy for Osteogenesis Imperfecta
- 27 May 2004
- journal article
- Published by Massachusetts Medical Society in New England Journal of Medicine
- Vol. 350 (22) , 2302-2304
- https://doi.org/10.1056/nejmcibr040806
Abstract
Targeting the collagen gene in bone mesenchymal stem cells can prevent the synthesis of mutant collagen and therefore represents a potential strategy for the treatment of diseases such as osteogenesis imperfecta.Keywords
This publication has 5 references indexed in Scilit:
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