Variation of Clinical Expression in Patients With Stargardt Dystrophy and Sequence Variations in the ABCRGene

Abstract
A GENE ASSOCIATED with Stargardt dystrophy1 and fundus flavimaculatus2 has been mapped to the short arm of chromosome 1. This gene was subsequently identified to be a photoreceptor gene–specific ATP-binding transporter gene (ABCR)3 that is localized to the disc membrane of retinal rod outer segments.4 Sequence changes in this gene were also identified in patients with age-related macular degeneration5 and in a family with an autosomal-recessive form of retinitis pigmentosa.6