C-Terminal-Truncated Microdystrophin Recruits Dystrobrevin and Syntrophin to the Dystrophin-Associated Glycoprotein Complex and Reduces Muscular Dystrophy in Symptomatic Utrophin/Dystrophin Double-Knockout Mice
Open Access
- 1 July 2006
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 14 (1) , 79-87
- https://doi.org/10.1016/j.ymthe.2006.01.007
Abstract
No abstract availableKeywords
This publication has 46 references indexed in Scilit:
- Viral serotype and the transgene sequence influence overlapping adeno‐associated viral (AAV) vector‐mediated gene transfer in skeletal muscleThe Journal of Gene Medicine, 2005
- Efficient in vivo gene expression by trans-splicing adeno-associated viral vectorsNature Biotechnology, 2005
- Phenotypic Improvement of Dystrophic Muscles by rAAV/Microdystrophin Vectors Is Augmented by Igf1 CodeliveryPublished by Elsevier ,2005
- Cardiomyopathy in dystrophin-deficient hearts is prevented by expression of a neuronal nitric oxide synthase transgene in the myocardiumHuman Molecular Genetics, 2005
- Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6Molecular Therapy, 2004
- Microdystrophin Gene Therapy of Cardiomyopathy Restores Dystrophin-Glycoprotein Complex and Improves Sarcolemma Integrity in the Mdx Mouse HeartCirculation, 2003
- Vasomodulation by Skeletal Muscle–Derived Nitric Oxide Requires α-Syntrophin–Mediated Sarcolemmal Localization of Neuronal Nitric Oxide SynthaseCirculation Research, 2003
- Expanding AAV Packaging Capacity with Trans-splicing or Overlapping Vectors: A Quantitative ComparisonMolecular Therapy, 2001
- Syntrophin Isoforms at the Neuromuscular Junction: Developmental Time Course and Differential LocalizationMolecular and Cellular Neuroscience, 2000
- Sexing of Mouse Preimplantation Embryos by Detection of Y Chromosome-Specific Sequences Using Polymerase Chain Reaction1Biology of Reproduction, 1992