Correction of ADAMTS13 Deficiency by In Utero Gene Transfer of Lentiviral Vector encoding ADAMTS13 Genes

This publication has 48 references indexed in Scilit:

• Factor VIII accelerates proteolytic cleavage of von Willebrand factor by ADAMTS13
  Proceedings of the National Academy of Sciences, 2008
• Platelet-VWF complexes are preferred substrates of ADAMTS13 under fluid shear stress
  Blood, 2008
• Efficient In Vivo Targeting of Epidermal Stem Cells by Early Gestational Intraamniotic Injection of Lentiviral Vector Driven by the Keratin 5 Promoter
  Molecular Therapy, 2008
• The cooperative activity between the carboxyl-terminal TSP1 repeats and the CUB domains of ADAMTS13 is crucial for recognition of von Willebrand factor under flow
  Blood, 2007
• Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells
  Nature Medicine, 2006
• Apical sorting of ADAMTS13 in vascular endothelial cells and Madin-Darby canine kidney cells depends on the CUB domains and their association with lipid rafts
  Blood, 2006
• Increased ADAMTS‐13 proteolytic activity in rat hepatic stellate cells upon activation in vitro and in vivo
  Journal of Thrombosis and Haemostasis, 2006
• Factor VIII ectopically expressed in platelets: efficacy in hemophilia A treatment
  Blood, 2003
• Modulation of Endothelial Cell Synthesis of von Willebrand Factor by Mononuclear Cell Products
  Pathophysiology of Haemostasis and Thrombosis, 1988
• Unusually Large Plasma Factor VIII: von Willebrand Factor Multimers in Chronic Relapsing Thrombotic Thrombocytopenic Purpura
  New England Journal of Medicine, 1982