Oligonucleotides against a splicing enhancer sequence led to dystrophin production in muscle cells from a Duchenne muscular dystrophy patient
- 31 December 2001
- journal article
- research article
- Published by Elsevier in Brain & Development
- Vol. 23 (8) , 788-790
- https://doi.org/10.1016/s0387-7604(01)00326-6
Abstract
No abstract availableKeywords
Funding Information
- National Center of Neurology and Psychiatry
- Ministry of Education, Culture, Sports, Science and Technology
- Ministry of Health, Labour and Welfare
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