Glycogen storage disease types I and II: Treatment updates
- 16 February 2007
- journal article
- review article
- Published by Wiley in Journal of Inherited Metabolic Disease
- Vol. 30 (2) , 159-164
- https://doi.org/10.1007/s10545-007-0519-9
Abstract
Prior to 2006 therapy for glycogen storage diseases consisted primarily of dietary interventions, which in the case of glycogen storage disease (GSD) type II (GSD II; Pompe disease) remained essentia...Keywords
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