AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice
Open Access
- 1 July 2004
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 10 (1) , 106-116
- https://doi.org/10.1016/j.ymthe.2004.03.018
Abstract
No abstract availableKeywords
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