Enzyme replacement therapy in an adolescent with Fabry disease
- 6 May 2003
- journal article
- Published by Springer Nature in European Journal of Pediatrics
- Vol. 162 (7-8) , 522-523
- https://doi.org/10.1007/s00431-003-1222-y
Abstract
No abstract availableKeywords
This publication has 6 references indexed in Scilit:
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- Safety and Efficacy of Recombinant Human α-Galactosidase A Replacement Therapy in Fabry's DiseaseNew England Journal of Medicine, 2001
- Enzyme Replacement Therapy in Fabry DiseaseJAMA, 2001
- A Phase 1/2 Clinical Trial of Enzyme Replacement in Fabry Disease: Pharmacokinetic, Substrate Clearance, and Safety StudiesAmerican Journal of Human Genetics, 2001
- Fabry Disease (α-Galactosidase A Deficiency)Published by Elsevier ,2001
- Enzymatic Defect in Fabry's DiseaseNew England Journal of Medicine, 1967