The role of gene therapy in haemophilia

This publication has 15 references indexed in Scilit:

• Adenovirus mediated expression of therapeutic plasma levels of human factor IX in mice
  Nature Genetics, 1993
• In Vivo Gene Therapy of Hemophilia B: Sustained Partial Correction in Factor IX-Deficient Dogs
  Science, 1993
• Toward Gene Therapy for Hemophilia A: Long-Term Persistence of Factor VIII-Secreting Fibroblasts after Transplantation into Immunodeficient Mice
  Human Gene Therapy, 1993
• Towards gene therapy for haemophilia B using primary human keratinocytes
  Nature Genetics, 1993
• Gene therapy via primary myoblasts: long-term expression of factor IX protein following transplantation in vivo.
  Proceedings of the National Academy of Sciences, 1992
• Gene therapy for human inherited disorders: techniques and status
  Critical Reviews in Oncology/Hematology, 1992
• Expression of human factor IX in rat capillary endothelial cells: toward somatic gene therapy for hemophilia B.
  Proceedings of the National Academy of Sciences, 1991
• Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs.
  Proceedings of the National Academy of Sciences, 1990
• Direct Gene Transfer into Mouse Muscle in Vivo
  Science, 1990
• An alternative approach to somatic cell gene therapy.
  Proceedings of the National Academy of Sciences, 1988