Retroviral vector design studies toward hematopoietic stem cell gene therapy for mucopolysaccharidosis type I
- 1 November 2000
- journal article
- research article
- Published by Springer Nature in Gene Therapy
- Vol. 7 (21) , 1875-1883
- https://doi.org/10.1038/sj.gt.3301298
Abstract
At the forefront of medicine, Gene Therapy brings you the latest research into genetic and cell-based technologies to treat disease. It also publishes Progress & Prospects reviews and News and Commentary articles, which highlight the cutting edge of the field.Keywords
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