Neurological Correction of Lysosomal Storage in a Mucopolysaccharidosis IIIB Mouse Model by Adeno-associated Virus-Mediated Gene Delivery
Open Access
- 1 January 2002
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 5 (1) , 42-49
- https://doi.org/10.1006/mthe.2001.0514
Abstract
No abstract availableKeywords
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