Eight years experience with enzyme replacement therapy in two children and one adult with Pompe disease
- 30 June 2008
- journal article
- case report
- Published by Elsevier in Neuromuscular Disorders
- Vol. 18 (6) , 447-452
- https://doi.org/10.1016/j.nmd.2008.04.009
Abstract
No abstract availableKeywords
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