In Situ Genetic Correction of the Sickle Cell Anemia Mutation in Human Induced Pluripotent Stem Cells Using Engineered Zinc Finger Nucleases

Abstract
The combination of induced pluripotent stem cell (iPSC) technology and targeted gene modification by homologous recombination (HR) represents a promis
Funding Information
  • NIH (R01 GM069906)
  • Pioneer Award (DP1 OD006862)
  • National Science Foundation Graduate Research fellowships
  • Start-up funds of the Institute for Stem Cell Biology and Regenerative Medicine
  • Stanford University School of Medicine and the Donald E. and Delia B. Baxter Foundation
  • CIRM Training Grant for postdoctoral fellows
  • New York Stem Cell Foundation Robertson Investigator
  • Jim and Ann Orr Massachusetts General Hospital Research Scholar