In Situ Genetic Correction of the Sickle Cell Anemia Mutation in Human Induced Pluripotent Stem Cells Using Engineered Zinc Finger Nucleases
Top Cited Papers
- 25 October 2011
- journal article
- research article
- Published by Oxford University Press (OUP) in The International Journal of Cell Cloning
- Vol. 29 (11) , 1717-1726
- https://doi.org/10.1002/stem.718
Abstract
The combination of induced pluripotent stem cell (iPSC) technology and targeted gene modification by homologous recombination (HR) represents a promisKeywords
Funding Information
- NIH (R01 GM069906)
- Pioneer Award (DP1 OD006862)
- National Science Foundation Graduate Research fellowships
- Start-up funds of the Institute for Stem Cell Biology and Regenerative Medicine
- Stanford University School of Medicine and the Donald E. and Delia B. Baxter Foundation
- CIRM Training Grant for postdoctoral fellows
- New York Stem Cell Foundation Robertson Investigator
- Jim and Ann Orr Massachusetts General Hospital Research Scholar
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