Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-label extension study
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- 1 April 2006
- journal article
- research article
- Published by Elsevier in The Journal of Pediatrics
- Vol. 148 (4) , 533-539.e6
- https://doi.org/10.1016/j.jpeds.2005.12.014
Abstract
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