Adenoviral-mediated expression of porphobilinogen deaminase in liver restores the metabolic defect in a mouse model of acute intermittent porphyria
Open Access
- 31 August 2004
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 10 (2) , 337-343
- https://doi.org/10.1016/j.ymthe.2004.05.018
Abstract
No abstract availableKeywords
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