SUCCESSFUL THERAPY OF NIEMANN-PICK DISEASE BY IMPLANTATION OF HUMAN AMNIOTIC MEMBRANE
- 1 July 1987
- journal article
- research article
- Published by Wolters Kluwer Health in Transplantation
- Vol. 44 (1) , 59-61
- https://doi.org/10.1097/00007890-198707000-00014
Abstract
In a patient with a lysosomal storage disorder, not involving the CNS, repeated implantations of human amniotic sheets have proved to provide a successful approach to enzyme replacement therapy. Implantation of pure epithelial cells, separated from the other cell types of the amnion, might markedly improve the procedure, avoiding some risks of host-versus-graft rejection.This publication has 9 references indexed in Scilit:
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