Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer
- 1 September 2001
- journal article
- Published by Springer Nature in Gene Therapy
- Vol. 8 (17) , 1291-1298
- https://doi.org/10.1038/sj.gt.3301420
Abstract
At the forefront of medicine, Gene Therapy brings you the latest research into genetic and cell-based technologies to treat disease. It also publishes Progress & Prospects reviews and News and Commentary articles, which highlight the cutting edge of the field.Keywords
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