AAV-Mediated expression of galactocerebrosidase in brain results in attenuated symptoms and extended life span in murine models of globoid cell leukodystrophy
Open Access
- 1 May 2005
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 11 (5) , 734-744
- https://doi.org/10.1016/j.ymthe.2004.12.020
Abstract
No abstract availableKeywords
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