Prevention of Dystrophin-Deficient Cardiomyopathy in Twenty-One-Month-Old Carrier Mice by Mosaic Dystrophin Expression or Complementary Dystrophin/Utrophin Expression
- 4 January 2008
- journal article
- research article
- Published by Wolters Kluwer Health in Circulation Research
- Vol. 102 (1) , 121-130
- https://doi.org/10.1161/circresaha.107.162982
Abstract
A cure for dystrophin-deficient muscular dystrophy requires treating both skeletal muscle and the heart. Whereas mosaic dystrophin expression has been shown to protect skeletal muscle, controversy ...Keywords
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