Mode of Action of RNA/DNA Oligonucleotides

This publication has 20 references indexed in Scilit:

• Longitudinal Follow-up of Patients With α1-Protease Inhibitor Deficiency Before and During Therapy With IV α1-Protease Inhibitor
  Chest, 2001
• Correction of the UDP-glucuronosyltransferase gene defect in the Gunn rat model of Crigler–Najjar syndrome type I with a chimeric oligonucleotide
  Proceedings of the National Academy of Sciences, 1999
• Gene Repair Using Chimeric RNA/DNA Oligonucleotides
  Seminars in Liver Disease, 1999
• Sustained secretion of human alpha-1-antitrypsin from murine muscle transduced with adeno-associated virus vectors
  Proceedings of the National Academy of Sciences, 1998
• In vivo site-directed mutagenesis of the factor IX gene by chimeric RNA/DNA oligonucleotides
  Nature Medicine, 1998
• Therapeutic gene targeting
  Gene Therapy, 1998
• Targeted nucleotide exchange in the alkaline phosphatase gene of HuH-7 cells mediated by a chimeric RNA/DNA oligonucleotide
  Hepatology, 1997
• Correction of the Mutation Responsible for Sickle Cell Anemia by an RNA-DNA Oligonucleotide
  Science, 1996
• Targeted gene correction of episomal DNA in mammalian cells mediated by a chimeric RNA.DNA oligonucleotide.
  Proceedings of the National Academy of Sciences, 1996
• alpha 1-Antitrypsin: molecular pathology, leukocytes, and tissue damage.
  Journal of Clinical Investigation, 1986