Gene therapy: a strategy for the treatment of inherited muscle diseases?

This publication has 45 references indexed in Scilit:

• Muscle-Specific Promoters May Be Necessary for Adeno-Associated Virus-Mediated Gene Transfer in the Treatment of Muscular Dystrophies
  Human Gene Therapy, 2001
• Functional EGFP–dystrophin fusion proteins for gene therapy vector development
  Protein Engineering, Design and Selection, 2000
• Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease
  Science, 2000
• Modulation of Starling Forces and Muscle Fiber Maturity Permits Adenovirus-Mediated Gene Transfer to Adult Dystrophic (mdx) Mice by the Intravascular Route
  Human Gene Therapy, 2000
• Development of new techniques using genetic and tissue engineering for the treatment of severe heart failure
  Transplantation Proceedings, 2000
• The Use of Adeno-Associated Virus to Circumvent the Maturation-Dependent Viral Transduction of Muscle Fibers
  Human Gene Therapy, 2000
• High-efficiency, long-term cardiac expression of foreign genes in living mouse embryos and neonates.
  Circulation, 2000
• Expression of the Primary Coxsackie and Adenovirus Receptor Is Downregulated during Skeletal Muscle Maturation and Limits the Efficacy of Adenovirus-Mediated Gene Delivery to Muscle Cells
  Human Gene Therapy, 1999
• Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector
  Nature Medicine, 1999
• Electropermeabilization of skeletal muscle enhances gene transfer in vivo
  Gene Therapy, 1999