Enhanced Efficacy of an AAV Vector Encoding Chimeric, Highly Secreted Acid α-Glucosidase in Glycogen Storage Disease Type II
Open Access
- 1 December 2006
- journal article
- research article
- Published by Elsevier in Molecular Therapy
- Vol. 14 (6) , 822-830
- https://doi.org/10.1016/j.ymthe.2006.08.001
Abstract
No abstract availableKeywords
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