Concerns about the design of clinical trials for spinal muscular atrophy

• 1 September 2004
• journal article
• review article
• Published by Elsevier in Neuromuscular Disorders
• Vol. 14  (8-9) , 456-460
• https://doi.org/10.1016/j.nmd.2004.04.004

Abstract

Keywords

• CLINICAL TRIALS
• STRATEGY FOR EVALUATING
• SMN
• RATE OF DEGENERATION
• DESIGN
• COMPLICATIONS
• SLOWING OF THE RATE
• MUSCULAR ATROPHY