Nonallele-specific Silencing of Mutant and Wild-type Huntingtin Demonstrates Therapeutic Efficacy in Huntington's Disease Mice
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Open Access
- 1 June 2009
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 17 (6) , 1053-1063
- https://doi.org/10.1038/mt.2009.17
Abstract
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