Successful Treatment of UGT1A1 Deficiency in a Rat Model of Crigler–Najjar Disease by Intravenous Administration of a Liver-Specific Lentiviral Vector
Open Access
- 28 February 2006
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 13 (2) , 374-381
- https://doi.org/10.1016/j.ymthe.2005.09.022
Abstract
No abstract availableKeywords
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