Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins
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Open Access
- 1 May 2011
- journal article
- research article
- Published by Elsevier in Molecular Therapy
- Vol. 19 (5) , 876-885
- https://doi.org/10.1038/mt.2010.274
Abstract
No abstract availableKeywords
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