Gene therapy for the hemophilias

This publication has 71 references indexed in Scilit:

• Site-specific genomic integration produces therapeutic Factor IX levels in mice
  Nature Biotechnology, 2002
• Dangerous liaisons: the role of “danger” signals in the immune response to gene therapy
  Blood, 2002
• Lentiviral vectors containing the human immunodeficiency virus type-1 central polypurine tract can efficiently transduce nondividing hepatocytes and antigen-presenting cells in vivo
  Blood, 2002
• Influence of Vector Dose on Factor IX-Specific T and B Cell Responses in Muscle-Directed Gene Therapy
  Human Gene Therapy, 2002
• Chromosomal effects of adeno-associated virus vector integration
  Nature Genetics, 2002
• Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors
  Gene Therapy, 2001
• Muscle-Directed Gene Transfer and Transient Immune Suppression Result in Sustained Partial Correction of Canine Hemophilia B Caused by a Null Mutation
  Molecular Therapy, 2001
• Risk and Prevention of Anti-factor IX Formation in AAV-Mediated Gene Transfer in the Context of a Large Deletion of F9
  Molecular Therapy, 2001
• Gene therapy for hemophilia
  The Journal of Gene Medicine, 2001
• Gene therapy for hemophilia: hopes and hurdles
  Critical Reviews in Oncology/Hematology, 1998