HUNTER SYNDROME IN FEMALES - THERE AN AUTOSOMAL RECESSIVE FORM OF IDURONATE SULFATASE DEFICIENCY

  • 1 January 1977
    • journal article
    • research article
    • Vol. 29  (5) , 455-461
Abstract
Profound iduronate sulfatase deficiency, characteristic of the Hunter syndrome, was found in cultured fibroblasts, serum, lymphocytes, and tissues of 2 clinically affected girls. The patients are karyotypically normal and have normal fathers; cloning of the mothers'' fibroblasts did not reveal the mosaicism expected of carriers of an X-linked disease. Homozygosity for a previously unsuspected autosomal recessive gene for iduronate sulfatase is considered the most likely explanation, although heterozygosity for the X-linked gene and subsequent selection cannot be completely excluded.