A Self-inactivating γ-Retroviral Vector Reduces Manifestations of Mucopolysaccharidosis I in Mice
Open Access
- 28 February 2010
- journal article
- Published by Elsevier in Molecular Therapy
- Vol. 18 (2) , 334-342
- https://doi.org/10.1038/mt.2009.236
Abstract
No abstract availableKeywords
Funding Information
- National Institute on Deafness and Other Communication Disorders (P30 DC004665, P30 NS057105, DK20579, DK066448, P30 DK52574, DK56341)
- National Institutes of Health (P30 DC004665, P30 NS057105, DK20579, DK066448, P30 DK52574, DK56341)
- National Institute of Neurological Disorders and Stroke (P30 DC004665, P30 NS057105, DK20579, DK066448, P30 DK52574, DK56341)
- National Institutes of Health (P30 DC004665, P30 NS057105, DK20579, DK066448, P30 DK52574, DK56341)
- University of Washington (P30 DC004665, P30 NS057105, DK20579, DK066448, P30 DK52574, DK56341)
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