Progress and Prospects: Gene Therapy Clinical Trials (Part 2)
- 6 November 2007
- journal article
- review article
- Published by Springer Nature in Gene Therapy
- Vol. 14 (22) , 1555-1563
- https://doi.org/10.1038/sj.gt.3303033
Abstract
This is the second part of a review summarizing progress and prospects in gene therapy clinical research. Twenty key diseases/strategies are succinctly described and commented on by leaders in the field. This part includes clinical trials for skin diseases, neurological disorders, HIV/AIDS, ornithine transcarbamylase deficiency, 1-antitrypsin deficiency, haemophilia and cancer.Keywords
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