Correction of sickle cell disease by homologous recombination in embryonic stem cells
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Open Access
- 15 August 2006
- journal article
- Published by American Society of Hematology in Blood
- Vol. 108 (4) , 1183-1188
- https://doi.org/10.1182/blood-2006-02-004812
Abstract
Previous studies have demonstrated that sickle cell disease (SCD) can be corrected in mouse models by transduction of hematopoietic stem cells with lKeywords
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